Pipeline

Pipeline

We are committed to developing precision genetic therapies for cardiomyopathies, heart failure, and polycystic kidney diseases, with a platform architecture that enables expansion into other disease areas. We are advancing our pipeline in collaboration with strategic external partners.

Pharmaceutical Pipeline
Program
Discovery
Pre-Clinical
Phase 1
Commercial Rights
MONOGENIC CARDIOMYOPATHIES
Hypertrophic Cardiomyopathy (HCM)
DINA - 001
DINA - 003
Arrhythmogenic Cardiomyopathy (ARVC)
DINA - 002
Dilated Cardiomyopathy (DCM)
DINA - 004/005
DINA - 006
MONOGENIC RENAL DISEASES
Autosomal Dominant Polycystic Kidney Diseases
DINAK - 001
DINAK - 002
Glomerular Diseases
DINAK - 003
DINAK - 004